2 Results Sort by:
Novel Therapeutic Target for Fragile X Syndrome and Neurodevelopmental Disorders
Application Salvianolic acid C for treating Fragile X Syndrome (FXS). Key Benefits New therapeutic drug candidate for the treatment of FXS. Preliminary data in the laboratory in organoids treated with the drug showed rescued cell phenotypes known to be associated with the disease in humans. Potential to treat other neurodevelopmental disorders. Market...
Published: 9/3/2025       Contributor(s): Peng Jin, Chuan He, Zhongyu Zou
Compounds Show Promise in Suppressing Fragile X Toxicity
Application Compounds for the treatment of Fragile X-associated tremor/ataxia syndrome. Key Benefits 11 known, FDA approved drugs identified that reduced rCGG-mediated lethality to a certain degree. 3 of these drugs also rescued locomotion deficits. Technical Summary Fragile X syndrome (FXS) is the most common inheritable form of cognitive...
Published: 3/28/2025       Contributor(s): Peng Jin, Abrar Qurashi