Compounds for Suppressing Fragile X Premutation rCGG Repreat-Mediated Toxicity
Compounds for the treatment of Fragile X-associated tremor/ataxia syndrome.
11 known, FDA approved drugs identified that reduced rCGG-mediated lethality to a certain degree.
3 of these drugs also rescued locomotion deficits.
Fragile X syndrome (FXS) is the most common inheritable form of cognitive disabi...
Inventor(s): Peng Jin, Abrar Qurashi